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Search Results - leanne+adams
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Autoregulated MBNL Gene Therapy for Myotonic Dystrophy
Next-Generation Gene Therapy Vectors with Tunable, Tissue-Specific, and Auto-Regulated Expression for Superior Safety and Efficacy This technology introduces recombinant adeno-associated virus (rAAV) vectors engineered to enable precise, regulated expression of therapeutic genes. Recombinant viruses can deliver therapeutic gene expression constructs...
Published: 9/2/2025
|
Inventor(s):
Eric Wang
,
Andy Berglund
,
Elizabeth Delgado
,
Jana Jenquin
,
Derek Muscato
,
Ona McConnell
,
Leanne Adams
,
Maria Valero Quiros
Keywords(s):
Category(s):
Technology Classifications > Human Health Care > Therapeutics
,
Technology Classifications > Research Tools > Therapeutics