Search Results - susan+slaugenhuapt

1 Results Sort By:
Creation and Use of Kinetin Derivatives for Treating RNA Missplicing Diseases Such as Familial Dysautonomia
This technology includes the creation and use of compounds, including kinetin derivatives, that improve mRNA splicing in a cell for the treatment of disorders associated with misspliced mRNA, including familial dysautonomia (FD). FD, the best-known and most common member of a group of congenital sensory and autonomic neuropathies, affects neuronal development...
Published: 10/28/2024   |   Inventor(s): Juan Marugan, Susan Slaugenhuapt
Keywords(s): Derivatives, Kinetin, VEXXXX, WKXXXX, XEXXXX
Category(s): Application > Therapeutics, TherapeuticArea > Neurology